Impact of Enzyme Replacement Therapy on Patients with Late Onset Pompe Disease – Real World Data from a Developing Country

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Authors: Swasti Pal, Sunita Bijarnia-Mahay, Sheela Nampoothiri, Mamta Muranjan, NP Gupta, Sankar Vh, Sujatha Jagadeesh, Meenakshi Bhat, Sanjeeva Gn, Dhanya Yesodharan, Prerana Modani, Madhulika Kabra
+2 more Priya S. Kishnani, Ratna Dua Puri
Cited by: 1
References: 26

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Whipple's Disease and Interleukins

Publication details

Journal / source
The Indian Journal of Pediatrics
Publisher
Springer Science and Business Media LLC
Volume
93
Issue
S1
Pages
48–55
Publication date
6 July 2026
Language
EN