Overcoming size barriers in retinal gene therapy via lipid nanoparticle-mediated delivery of full-length eys DNA

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Authors: Sarah Goddaer, Emma De Coster, Elise Callens, Emma Van Caenegem, Olivier Van den Heule, Rob W.J. Collin, Karen Peynshaert, Filip Van Nieuwerburgh, Kevin Braeckmans, Katrien Remaut
Cited by: 0
References: 56

Fields of Study & Subjects

RNA Interference and Gene Delivery Retinal Development and Disorders Advanced Drug Delivery Systems

Publication details

Journal / source
Drug Delivery and Translational Research
Volume
16
Issue
8
Pages
2921–2936
Publication date
28 January 2026
Language
EN