Long-term reversal of Duchenne muscular dystrophy via circular arRNA-guided exon skipping in monkeys and humans

Cell 2026

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Authors: Wenting Guo, Huixian Tang, Zongyi Yi, Ting Zhang, Pengfei Yuan, Cuijin Wang, Shuaiwei Ren, 常希文, Jiwu Ren, W Tang, Wenjie Sun, J S Liu
+22 more Ying Yu, Zhiwei Lü, Hongyan Shen, Zexuan Yi, Yanxia Zhao, Tang Gangbin, Junyuan Han, Wenzhi Zhang, Haoyue Liu, Xueqing Sun, Yongjian Zhang, Cui Zhang, Yuming Wu, Ling Yang, Feng Han, Yichao Xu, Liang Qu, Xinyan Sun, Jiwen Wang, Weizhi Ji, Yongchang Chen, Wensheng Wei
DOI: 10.1016/j.cell.2026.05.030
Cited by: 4
References: 58

Fields of Study & Subjects

RNA regulation and disease Muscle Physiology and Disorders CRISPR and Genetic Engineering

Publication details

Journal / source
Cell
Publisher
Elsevier BV
Volume
189
Issue
14
Pages
4377–4395.e20
Publication date
10 June 2026
Language
EN