P114: Long-term safety and efficacy of pegunigalsidase alfa in patients with Fabry disease: Results from the phase 3 BRILLIANCE Extension Study*

Genetics in Medicine Open 2026 Open access

Read full text

Authors: John A. Bernat, Aleš Linhart, Özlem Göker-Alpan, Shoshi Tessler, Meng Wang, Giovanni Piotti, Joana Almeida, Derralynn A. Hughes

DOI: 10.1016/j.gimo.2026.103608

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders