Pharmacokinetically-Adjusted Busulfan Dosing in Adults and Adolescents with Sickle Cell Disease or Transfusion-Dependent β-Thalassemia Treated with Exagamglogene Autotemcel

Transplantation and Cellular Therapy 2026

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Authors: Haydar Frangoul, Akshay Sharma, Roland Meisel, Peter Lang, Selim Corbacioglu, Melanie Ann Kirby-Allen, Josu de la Fuente, Amanda Li, Lyndsay Molinari, Monica Bhatia, Robert I. Liem, Markus Y. Mapara
+9 more Stephan A. Grupp, Mark Peterson, Sakellarios Zairis, Laura Bower, Tina Liu, Suzan Imren, William Hobbs, Praveen Shukla, Franco Locatelli
DOI: 10.1016/j.jtct.2025.12.962
Cited by: 0

Fields of Study & Subjects

Hemoglobinopathies and Related Disorders Hematopoietic Stem Cell Transplantation Virus-based gene therapy research

Publication details

Journal / source
Transplantation and Cellular Therapy
Volume
32
Issue
2
Pages
S129–S130
Publication date
1 February 2026
Language
EN