PCR24 PATIENT DESCRIPTIONS OF IMPROVED ABILITY TO SELF-REGULATE BLOOD SUGAR LEVELS IN A PHASE 3 TRIAL OF DTX401 FOR GLYCOGEN STORAGE DISEASE TYPE IA

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Authors: Diane M. Turner‐Bowker, Shayna Egan, Blaise Cureg, Adriana Voci, Monica Boyer, Jessica Butler, Richard Collis, Elizabeth Dorn, Kristin N. Voorhees, Martha Gauthier
Cited by: 1

Fields of Study & Subjects

Glycogen Storage Diseases and Myoclonus Celiac Disease Research and Management Diabetes and associated disorders

Publication details

Journal / source
Value in Health
Publisher
Elsevier BV
Volume
29
Issue
6
Pages
S361–S361
Publication date
1 June 2026
Language
EN