Potential impact of early pharmacological treatment on gene therapy outcomes in AADC deficiency

Parkinsonism & Related Disorders 2026

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Authors: Mario Mastrangelo, Luca D’Angelo, Roberta Battini, Filippo Manti, Annamaria Gigliello, Maria Teresa Giannini, Federica D’Acunto, Paola Cristofani, Patrizia Maggiore, Antonio Angeloni, Antonio Santoro, Francesco Sergio Pisani
+1 more Vincenzo Leuzzi
DOI: 10.1016/j.parkreldis.2026.108253
Cited by: 0
References: 4

Fields of Study & Subjects

Virus-based gene therapy research Metabolism and Genetic Disorders Lysosomal Storage Disorders Research

Publication details

Journal / source
Parkinsonism & Related Disorders
Volume
145
Pages
108253–108253
Publication date
27 February 2026
Language
EN