Generation of induced pluripotent stem cell lines from three Marfan syndrome patients carrying mutations in the fibrillin-1 gene

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Authors: Philipp Christoph Hauger, Tyler J. Kirby, Maarten Groenink, Herak Manjikian, Vivian de Waard, Peter L. Hordijk
Cited by: 1
References: 5

Abstract

Marfan syndrome is a heritable connective tissue disorder associated with cardiovascular complications, including progressive aortic aneurysm and dissection, caused by mutations in the fibrillin-1 (FBN1) gene. We generated human induced pluripotent stem cells (hiPSCs) from skin fibroblasts of 3 patients carrying FBN1 mutations (FBN1 c.6554 T > C, FBN1 c.4425-4426delinsC, FBN1 c.6806 T > C) using an episomal vector reprogramming system. These hiPSC lines exhibit pluripotent stem cell morphology, express established markers of undifferentiated hPSC state, maintain a normal karyotype, and differentiation potential into the 3 germ layers. These hiPSC lines provide a cellular model to investigate Marfan syndrome and its associated cardiovascular pathology in vitro.

Fields of Study & Subjects

Connective tissue disorders research Congenital heart defects research Tendon Structure and Treatment

Publication details

Journal / source
Stem Cell Research
Publisher
Elsevier BV
Volume
95
Pages
104029–104029
Publication date
6 June 2026
Language
EN