Lipid nanoparticle-based non-viral in situ gene editing of congenital ichthyosis-causing mutations in human skin models

Cell stem cell 2026

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Authors: Dilem Ceren Apaydin, Gaurav Sadhnani, Tiffany Carlaw, Jan Renziehausen, Elena Lizunova, Viviane Filor, Anna Hiller, Sophia Brumhard, Vincent Halim, Ulrike Brüning, Johannes Bischof, Rafaela Horbach Marodin
+13 more Daniel Z. Kurek, Manuel Rhiel, Sandra Ammann, Tatjana I. Cornu, Toni Cathomen, Leif Erik Sander, Benedikt Obermayer, Fabian Coscia, Jennifer Kirwan, Ulrich Koller, Achim D. Gruber, Wolfgang Bäumer, Sarah Hedtrich
DOI: 10.1016/j.stem.2026.01.001
Cited by: 4
References: 115

Fields of Study & Subjects

Skin and Cellular Biology Research Nuclear Structure and Function Erythrocyte Function and Pathophysiology

Publication details

Journal / source
Cell stem cell
Publisher
Elsevier BV
Volume
33
Issue
2
Pages
233–252.e12
Publication date
27 January 2026
Language
EN