Serial brain MRI volumetrics and DTI analysis in atypical CLN2 patients treated with ICV cerliponase alfa

Molecular Genetics and Metabolism 2026

View at publisher

Authors: Sumiko Abe, Harriet Chang, Audrey Kao, Maija Steenari, Raymond Y. Wang

DOI: 10.1016/j.ymgme.2025.109299

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Metabolism and Genetic Disorders Glycogen Storage Diseases and Myoclonus