Advances in the administration of ERT (oral pathway) improving the biodistribution of enzymes

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Authors: José Víctor Álvarez González, Daniel Caiola, Cristobal Colon, Susana J. Bravo Lopez, Carmen Pena, Bruno K. Rodiño‐Janeiro, Francisco Javier Otero-Espinar, María Lourdes Couce
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Fields of Study & Subjects

Lysosomal Storage Disorders Research Metabolism and Genetic Disorders Glycogen Storage Diseases and Myoclonus

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109309–109309
Publication date
1 February 2026
Language
EN