followME Fabry Pathfinders real-world registry in Spain and Portugal: Cardiac and renal outcomes with migalastat in patients with Fabry disease

Molecular Genetics and Metabolism 2026

View at publisher
Authors: Olga M. Azevedo, Tomás Ripoll‐Vera, Patricio Aguiar, Roser Torrá, Vicente Climent-Payá, María Camprodón-Gómez, Joaquín de Juan-Ribera, Manuel Lopez Mendoza, Mario Espinosa, Jorge Martín, João-Paulo Oliveira, Elena Fortuny
+9 more José Manuel García‐Pinilla, Juan Ramón Gimeno, Francisco Javier Mena Martín, Ana Aguinaga, Ana Luisa Vaz, Jennifer Hiros, Vipul Jain, Biliana O. Veleva-Rotse, Vicent Torregrosa
DOI: 10.1016/j.ymgme.2025.109320
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109320–109320
Publication date
1 February 2026
Language
EN