Real-world utilization and adherence patterns of enzyme replacement therapy in Fabry disease: Survey results from 238 patients in the USA and Canada

Molecular Genetics and Metabolism 2026

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Authors: Lisa Berry, Irene N. Koulinska, Jerry Walter, Jack L. Johnson, Julia Alton, Janet Bernard, Swati Kunduri, Dawn A. Laney

DOI: 10.1016/j.ymgme.2025.109338

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders