Tividenofusp alfa treatment in a male sibling pair with non-neuronopathic mucopolysaccharidosis type II (MPS II)

Molecular Genetics and Metabolism 2026

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Authors: Irene Chang, Jacqueline Madden, Annie Sako, Jill K. Dwyer, Daniel Fertek, Adam Scheller, Sharon O’Byrne, Imanol Zubizarreta, Peter Chin, Paul Harmatz
DOI: 10.1016/j.ymgme.2025.109363
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109363–109363
Publication date
1 February 2026
Language
EN