GAA-based therapeutic strategies for neurological glycogen storage diseases

Molecular Genetics and Metabolism 2026

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Authors: Matthieu G. Colpaert, Pankaj K. Singh, Tiantian Chen, Lei Wu, Alex R. Cantrell, Yueying Liu, Ramon C. Sun, Craig W. Vander Kooi, Matthew S. Gentry
DOI: 10.1016/j.ymgme.2025.109372
Cited by: 0

Fields of Study & Subjects

Glycogen Storage Diseases and Myoclonus Lysosomal Storage Disorders Research Virus-based gene therapy research

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109372–109372
Publication date
1 February 2026
Language
EN