Mucopolysaccharidosis type II: Brain and spine MRI in patients treated with idursulfase
Fields of Study & Subjects
Lysosomal Storage Disorders Research
Glycogen Storage Diseases and Myoclonus
Neurogenetic and Muscular Disorders Research
Publication details
- Journal / source
- Molecular Genetics and Metabolism
- Volume
- 147
- Issue
- 2
- Pages
- 109377–109377
- Publication date
- 1 February 2026
- Language
- EN