Dual site administration of AAV gene therapy for treatment of feline GM1 gangliosidosis

Molecular Genetics and Metabolism 2026

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Authors: Courtney Garrett, Juan Rodriguez, Douglas R. Martin, Amanda L. Gross
DOI: 10.1016/j.ymgme.2025.109419
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Virus-based gene therapy research RNA Interference and Gene Delivery

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109419–109419
Publication date
1 February 2026
Language
EN