Intravenous hydroxypropyl-beta-cyclodextrin (HPBCD): Biomarkers, efficacy, and impact of dosing and administration route on therapeutic index

Molecular Genetics and Metabolism 2026

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Authors: Caroline A. Hastings, Benny Liu, Thorsten Marquardt

DOI: 10.1016/j.ymgme.2025.109457

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Drug Solubulity and Delivery Systems Metabolism and Genetic Disorders