A transfusion related adverse event attributed to IgA2 driven complement activation is observed in two Fabry disease patients given α-galactosidase based enzyme replacement therapy
Fields of Study & Subjects
Lysosomal Storage Disorders Research
Complement system in diseases
Blood transfusion and management
Publication details
- Journal / source
- Molecular Genetics and Metabolism
- Volume
- 147
- Issue
- 2
- Pages
- 109462–109462
- Publication date
- 1 February 2026
- Language
- EN