Caregiver treatment preferences in late infantile and early juvenile metachromatic leukodystrophy: A best-worst scaling study

Molecular Genetics and Metabolism 2026

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Authors: Ellen M. Howard, Elin Gruffydd, Karen Bean, Francis Pang, Annamarie Dillon, Gin Nie Chua

DOI: 10.1016/j.ymgme.2025.109470

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Family and Disability Support Research Metabolism and Genetic Disorders