Novel cyclodextrins enhance potency of neutralization and clearance of endogenous psychosine in cellular and in vivo models of Krabbe disease

Molecular Genetics and Metabolism 2026

View at publisher

Authors: Shih‐Chang Hsueh, Jayar Espejo, Ping Zhang, Ezra M. Yohannan Cheria, Renu Nandakumar, Chang‐Chun Ling, Gustavo H. B. Maegawa

DOI: 10.1016/j.ymgme.2025.109471

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Biomedical Research and Pathophysiology