Long-term effectiveness and safety of agalsidase alfa in patients with Fabry disease treated for at least 19 years: The Fabry Outcome Survey

Molecular Genetics and Metabolism 2026

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Authors: Derralynn A. Hughes, Guillem Pintos‐Morell, Kathy Nicholls, Dau-Ming Niu, Michael L. West, Jaco Botha, Alan Caro, Ricardo Claudio Reisin, Roberto Giugliani
DOI: 10.1016/j.ymgme.2025.109477
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109477–109477
Publication date
1 February 2026
Language
EN