Biochemical and enzymatic evaluation on the clinical efficacy of migalastat for Fabry disease

Molecular Genetics and Metabolism 2026

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Authors: Masahisa Kobayashi, Hiroshi Kobayashi

DOI: 10.1016/j.ymgme.2025.109505

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders