Changing natural history: A case series of causes of death in individuals with classic Fabry disease who began primary therapy later in disease progression

Molecular Genetics and Metabolism 2026

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Authors: Dawn A. Laney, Alaena Lim, Erin Kistenberg, Eleanor G. Botha, Mari Mori, William R. Wilcox

DOI: 10.1016/j.ymgme.2025.109515

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders