Quality of life (QoL), unmet needs, and treatment experience of people living with mucopolysaccharidosis type II (MPS II) and their caregivers: A community survey

Molecular Genetics and Metabolism 2026

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Authors: Kristin McKay, Stefan Anghel, Sydney Gardner

DOI: 10.1016/j.ymgme.2025.109546

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Family and Disability Support Research Neurogenetic and Muscular Disorders Research