followME Fabry Pathfinders registry: Cardiac and renal effectiveness in a multi-national, multi-center cohort of patients on migalastat treatment for 5 years

Molecular Genetics and Metabolism 2026

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Authors: Peter Nordbeck, Joseph D. Giuliano, Aleš Linhart, Antonio Pisani, Olga M. Azevedo, Jennifer Hiros, Vipul Jain, Biliana O. Veleva-Rotse, Derralynn A. Hughes
DOI: 10.1016/j.ymgme.2025.109564
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Metabolism and Genetic Disorders Glycogen Storage Diseases and Myoclonus

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109564–109564
Publication date
1 February 2026
Language
EN