DYNE-401 demonstrates potential to address Pompe disease with low and infrequent dosing

Molecular Genetics and Metabolism 2026

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Authors: Tyler Picariello, Ann (Ya-An) Chang, Lydia Schlaefke, Jennifer Johnson, Stephanie Rinaldi, Blanca Lain, Nicholas C. Yoder, Oxana Ibraghimov‐Beskrovnaya, Ranjan Batra, Stefano Zanotti
DOI: 10.1016/j.ymgme.2025.109581
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Biomedical Research and Pathophysiology

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109581–109581
Publication date
1 February 2026
Language
EN