Gaucher teen and young adult Washington DC advocacy program focuses on unmet needs and policy concerns affecting rare disease

Molecular Genetics and Metabolism 2026

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Authors: Aviva Rosenberg, Cynthia Frank, Madelyn Schloss

DOI: 10.1016/j.ymgme.2025.109600

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders