Next-generation enzyme replacement strategies for Gaucher disease

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Authors: Pau Sarlé Vallés, Eddi Pradas Gracia, Pablo Castillo-Sanchez, Sebastián Tanco, Mercedes Arrúe, Marta Artola, Maria Jesus Vicent, Marta Martínez‐Vicente, Júlia Lorenzo
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Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109610–109610
Publication date
1 February 2026
Language
EN