A comprehensive analysis of medication switching in type 1 Gaucher disease

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Authors: Karolina M. Stępień, Mia Giles, Asmaa Alzuabi, Reena Sharma, Ana Jovanović, Mairead A. Jones
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Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109633–109633
Publication date
1 February 2026
Language
EN