Characterization of bone and joint cell models of MPS II generated through CRISPR/Cas9 technology

Molecular Genetics and Metabolism 2026

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Authors: Emilio Vaena, Romina Ceci, Maria C. Alvarez, Paula A. Rozenfeld
DOI: 10.1016/j.ymgme.2025.109651
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus CRISPR and Genetic Engineering

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109651–109651
Publication date
1 February 2026
Language
EN