Global characterization of GM1 gangliosidosis: Insights from a patient-powered registry

Molecular Genetics and Metabolism 2026

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Authors: Christine Waggoner, Scott Milligan, Dee-Anne Breault

DOI: 10.1016/j.ymgme.2025.109658

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders