Enhanced CIMPR binding and cellular uptake of HP-GALNS (M161): A next-generation enzyme replacement therapy for Morquio syndrome type A

Molecular Genetics and Metabolism 2026

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Authors: Udayanga S. Wanninayake, Jonathan Roberts, Shou Liu, Michael R. DiGruccio, Linda E. Winter, Linda Lyons, Riley N. Marcinczyk, Andrew C. Hedman, Qi Gan, Russell R. Gotschall, Adriana M. Montaño
DOI: 10.1016/j.ymgme.2025.109662
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Proteoglycans and glycosaminoglycans research

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109662–109662
Publication date
1 February 2026
Language
EN