Long-term outcome of Hurler syndrome following bone marrow transplantation

Molecular Genetics and Metabolism 2026

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Authors: Chester B. Whitley, Kumar G. Belani, Elizabeth Braunlin, Paul J. Orchard, Jeanine R. Jarnes, Alia Ahmed, Brenda M. Diethelm-Okita

DOI: 10.1016/j.ymgme.2025.109670

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Metabolism and Genetic Disorders