Global insights into parental perception of treatment options for mucopolysaccharidosis: A collaborative international survey for advancing clinical trials

Molecular Genetics and Metabolism 2026

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Authors: Anna‐Maria Wiesinger, Mirko M. Essing, Roberto Giugliani, Hernán M. Amartino, Mireia del Toro, Beate Priewasser, Martin Magner, John J. Mitchell
DOI: 10.1016/j.ymgme.2025.109672
Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Family and Disability Support Research Neurogenetic and Muscular Disorders Research

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
2
Pages
109672–109672
Publication date
1 February 2026
Language
EN