A progranulin derivative blocks the C5a/C5aR1 signaling and mitigates pathology in Gaucher disease

Molecular Genetics and Metabolism 2026

View at publisher

Authors: Xiangli Zhao, Wenyu Fu, Yi Lin, Benjamin Liou, Venette Fannin, Gregory A. Grabowski, Ying Sun, C.-J. Liu

DOI: 10.1016/j.ymgme.2025.109683

Cited by: 0

Fields of Study & Subjects

Lysosomal Storage Disorders Research Glycogen Storage Diseases and Myoclonus Complement system in diseases