Doxecitine and doxribtimine for the treatment of TK2 deficiency: FDA approval summary
Fields of Study & Subjects
Metabolism and Genetic Disorders
Biochemical and Molecular Research
Lysosomal Storage Disorders Research
Publication details
- Journal / source
- Molecular Genetics and Metabolism
- Volume
- 147
- Issue
- 3
- Pages
- 109735–109735
- Publication date
- 12 February 2026
- Language
- EN