Sepiapterin for the treatment of PKU: FDA approval summary
Fields of Study & Subjects
Metabolism and Genetic Disorders
Lysosomal Storage Disorders Research
Amino Acid Enzymes and Metabolism
Publication details
- Journal / source
- Molecular Genetics and Metabolism
- Volume
- 147
- Issue
- 4
- Pages
- 109863–109863
- Publication date
- 26 February 2026
- Language
- EN