Sepiapterin for the treatment of PKU: FDA approval summary

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Authors: Jamie Rosenthal
Cited by: 0
References: 3

Fields of Study & Subjects

Metabolism and Genetic Disorders Lysosomal Storage Disorders Research Amino Acid Enzymes and Metabolism

Publication details

Journal / source
Molecular Genetics and Metabolism
Volume
147
Issue
4
Pages
109863–109863
Publication date
26 February 2026
Language
EN