Gene therapy for Bietti crystalline corneoretinal dystrophy: A phase 1/2 clinical trial

Molecular Therapy 2026 Open access

Read full text
Authors: Liping Yang, Dongjun Xing, Jinlu Zhang, Boshi Liu, Xiaoshuang Jiang, Shaohong Chen, Wang Li, Baoyuan Qu, Jing Qiao, Xuefeng Feng, Haicun Jia, Xianjun Hu
+7 more Shicheng Yu, Ruixuan Jia, Likun Wang, Vinit B. Mahajan, Hongliang Dou, Fang Lu, Xiaorong Li
DOI: 10.1016/j.ymthe.2026.01.005
Cited by: 2
References: 46

Fields of Study & Subjects

Retinal Development and Disorders Retinal Diseases and Treatments Retinal and Macular Surgery

Publication details

Journal / source
Molecular Therapy
Publisher
Elsevier BV
Volume
34
Issue
3
Pages
1743–1755
Publication date
10 January 2026
Language
EN