Safety and efficacy of hemobeglogene autotemcel(hemo-cel) gene therapy in five patients with transfusion-dependent β-thalassemia

Molecular Therapy 2026 Open access

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Authors: Sixi Liu, Yue Chen, Yue Li, Linxia Qian, Guoyi Dong, Qian Zhang, Xiaohui Zhou, Honglian Guo, Haigang Sun, Qihong Lin, Jiaming Yu, Xinru Zeng
+5 more Huilin Zou, Jiajun He, Wenwen Yao, Wenjie Ouyang, Chao Liu
DOI: 10.1016/j.ymthe.2026.02.017
Cited by: 1
References: 31

Fields of Study & Subjects

Hemoglobinopathies and Related Disorders Virus-based gene therapy research Xenotransplantation and immune response

Publication details

Journal / source
Molecular Therapy
Publisher
Elsevier BV
Volume
34
Issue
5
Pages
2611–2620
Publication date
14 February 2026
Language
EN