Who will win the race for the first CFTR gene replacement therapy?

Molecular Therapy 2026 Open access

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Authors: John J. Brewington, Marcus A. Mall, Yutaka Maeda

DOI: 10.1016/j.ymthe.2026.02.025

Cited by: 1

References: 9

Fields of Study & Subjects

Cystic Fibrosis Research Advances Virus-based gene therapy research Endoplasmic Reticulum Stress and Disease

References 9