Imlifidase enables AAV gene therapy in a seropositive Crigler-Najjar patient: On the verge of a paradigm shift

Molecular Therapy 2026 Open access

Read full text
Authors: Jérémy Do Cao, Ji Gao-Desliens, Arnaud Valent, Nathalie Knuchel-Legendre, Claire Colpin, Hélène Guyon, Lena Winstedt, Christian Leborgne, Gérald Perret, Giuseppe Ronzitti, Philippe Labrune
DOI: 10.1016/j.ymthe.2026.04.018
Cited by: 1
References: 5

Fields of Study & Subjects

Virus-based gene therapy research Lysosomal Storage Disorders Research Neurogenetic and Muscular Disorders Research

Publication details

Journal / source
Molecular Therapy
Publisher
Elsevier BV
Volume
34
Issue
5
Pages
2571–2572
Publication date
27 April 2026
Language
EN