Safety and efficacy of fordadistrogene movaparvovec in ambulatory participants with Duchenne muscular dystrophy (CIFFREO): a phase 3, double-blind, randomised, placebo-controlled study

The Lancet Neurology 2026

View at publisher
Authors: Francesco Muntoni, Andres Nascimento, Jinhong Shin, Michela Guglieri, Georg M. Stettner, Aravindhan Veerapandiyan, Silvina Gallo, Heliang Shi, Balarama Gundapaneni, Srividya Neelakantan, Kasia Lobello, Qi Shen
+2 more David Lévy, Eugenio Mercuri
DOI: 10.1016/s1474-4422(26)00036-0
Cited by: 2
References: 20

Fields of Study & Subjects

Muscle Physiology and Disorders Pain Management and Treatment Adipose Tissue and Metabolism

Publication details

Journal / source
The Lancet Neurology
Publisher
Elsevier BV
Volume
25
Issue
3
Pages
245–255
Publication date
18 February 2026
Language
EN