Broad lessons from negative trials in rare diseases

The Lancet Neurology 2026

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Authors: Laurent Servais, Maryam Saket Oskoui

DOI: 10.1016/s1474-4422(26)00038-4

Cited by: 1

References: 7

Fields of Study & Subjects

Virus-based gene therapy research Muscle Physiology and Disorders Neurogenetic and Muscular Disorders Research

References 7