Safety, tolerability, and efficacy of RIPK1 inhibitor, SAR443820, in amyotrophic lateral sclerosis (HIMALAYA): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial

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Authors: Merit Cudkowicz, Merit E Cudkowicz, Jeremy Shefner, Leonard H van den Berg, Adriano Chio, Dongsheng Fan, Julian Großkreutz, Christian Lunetta, Richard M Tsai, Ye Li, Erik Wallstroem, Li Xiong
+88 more Yixin Chen, Nazem Atassi, Kristl Claeys, Philip Van Damme, Philippe Beauchemin, Annie Dionne, Oliver Blanchard, Angela Genge, Rami Massie, Jeanne Teitelbaum, Grayson Beecher, Peter Dobrowolski, Wendy Johnston, Michael Nicolle, Christen Shoesmith, Marvin Chum, John Turnbull, Agessandro Abrahão, Antonio Saldanha De Castro Perdo, Isaac Hughes, Dhruv Kumar Jain, Denizart Santos Neto, Lorne Zinman, Yong Chen, Dongsheng Fan, Ji He, Xin Huang, Xiaolu Liu, Yan Ma, Xinyu Zhang, Chen Zhao, Mei Zheng, Hongfu Li, Hao Yu, Hao Yu, Chunyu Li, Huifang Shang, Qianqian Wei, Yi Xiao, Tianmi Yang, Yang Liu, Yang Liu, Min Zhang, Haishan Jiang, Hui Zheng, Jingxia Dang, Jiaoting Jin, Jiaoting Jin, Shahram Attarian, Aude‐Marie Grapperon, Annie Verschueren, Elisa De la Cruz, Alix Durand, Florence Esselin, Stephane Beltran, Philippe Corcia, Valérie Gissot, Pauline Ducatel, Maud Michaud, Sophie Pittion Vouyovitch, Veronique Danel Brunaud, Celine Tard, Charlotte Arnaud, Julien Cogez, Mathilde Lefilliatre, Johannes Dorst, Andrea Fromm, Albert Ludolph, Oezlem Parlak, Ulrike Weiland, Maximilian Wiesenfarth, Norbert Brueggemann, Carolina Gerke, Julian Grosskreutz, Meret Herdick, Simon Schuster, Alica Teroerde, Janina von der Gablentz, Bjoern Falkenburger, René Guenther, Hanna Lapp, Maximilian Vidovic, Constanze Weber, Dagmar Kettemann, Andre Maier, Thomas Meyer, Sonja Koerner, Susanne Petri
Cited by: 1
References: 29

Fields of Study & Subjects

Amyotrophic Lateral Sclerosis Research Neurogenetic and Muscular Disorders Research Hereditary Neurological Disorders

Publication details

Journal / source
The Lancet Neurology
Publisher
Elsevier BV
Volume
25
Issue
10
Pages
900–910
Publication date
9 September 2026
Language
EN