Safety of in vivo gene therapy in children: mechanisms and management of liver injury

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Authors: Rebecca Jeyaraj, Li-An K. Brown, Barath Jagadisan, Francesco Muntoni, Julien Baruteau, Girish Gupte, Judith Breuer, Paul Gissen, Ye H Oo, A. K. Dhawan
Cited by: 4
References: 88

Fields of Study & Subjects

Virus-based gene therapy research CRISPR and Genetic Engineering Nerve injury and regeneration

Publication details

Journal / source
The Lancet Child & Adolescent Health
Publisher
Elsevier BV
Volume
10
Issue
6
Pages
448–461
Publication date
9 February 2026
Language
EN