Real-life effectiveness and safety of lumacaftor/ivacaftor in preschool children with cystic fibrosis: data from an italian multicentre study

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Authors: Santiago Presti, Chiara Cimbalo, Alberto Terminiello, Cristina Fevola, Valeria Daccò, Angela Sepe, Patrizia Troiani, Rosaria Casciaro, Noemi Di Dio, Chiara Castellani, Iréne Esposito, Francesca Ficili
+5 more Domenica De Venuto, Maria Adelaide Calderazzo, Pietro Ripani, Donatello Salvatore, Vito Terlizzi
Cited by: 1
References: 48

Fields of Study & Subjects

Cystic Fibrosis Research Advances Pediatric health and respiratory diseases Chemical and Physical Studies

Publication details

Journal / source
Pediatric Research
Publisher
Springer Science and Business Media LLC
Publication date
22 May 2026
Language
EN