Clinical application of base editing for treating β-thalassaemia

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Authors: Yongrong Lai, Rongrong Liu, Lijie Wang, Xu-Kai Ma, Yaliang Li, Gaohui Yang, Lingling Shi, Yilin Guo, Zhenbin Wei, X. K. Zhou, Wenchao Xu, Yaofeng Hou
+5 more Annarita Miccio, Bei Yang, Xiaodun Mou, Li Yang, J. L. Chen
Cited by: 8
References: 63

Fields of Study & Subjects

Hemoglobinopathies and Related Disorders Hematopoietic Stem Cell Transplantation Blood groups and transfusion

Publication details

Journal / source
Nature
Publisher
Springer Science and Business Media LLC
Volume
653
Issue
8115
Pages
923–932
Publication date
8 April 2026
Language
EN