The impact of antisense oligonucleotide (ASO) therapeutics on the future of rare disease drug discovery

Expert Opinion on Drug Discovery 2026 Open access

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Authors: Ruchi Ruchi, Kriti Gupta, Rajkumar Verma, José Enrique Manautou, Xiao-B Zhong, Raman Bahal
DOI: 10.1080/17460441.2026.2652440
Cited by: 5
References: 23

Abstract

1. Recent advances in nucleic acid therapeutics (NAT) have fundamentally changed the treatment aspect for genetic diseases, indicating that precise intervention at the DNA or RNA level can result i...

Fields of Study & Subjects

DNA and Nucleic Acid Chemistry Genomics and Rare Diseases Genomic variations and chromosomal abnormalities

Publication details

Journal / source
Expert Opinion on Drug Discovery
Publisher
Informa UK Limited
Volume
21
Issue
4
Pages
369–373
Publication date
27 March 2026
Language
EN