Precision medicine in the era of CFTR modulator therapy: what comes next?
Abstract
Extract Cystic fibrosis (CF) is an inherited disease that affects multiple organs, including the lungs and airways, pancreas, liver and the gut. CF is caused by cystic fibrosis transmembrane conductance regulator (CFTR) dysfunction, leading to impaired chloride ion transport across membranes [1, 2.
Fields of Study & Subjects
Cystic Fibrosis Research Advances
Endoplasmic Reticulum Stress and Disease
Occupational and environmental lung diseases
Publication details
- Journal / source
- European Respiratory Journal
- Publisher
- European Respiratory Society (ERS)
- Volume
- 67
- Issue
- 6
- Pages
- 2600247–2600247
- Publication date
- 1 June 2026
- Language
- EN