Precision medicine in the era of CFTR modulator therapy: what comes next?

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Authors: José Fontoura Matias, Hartmut Grasemann
Cited by: 1
References: 19

Abstract

Extract Cystic fibrosis (CF) is an inherited disease that affects multiple organs, including the lungs and airways, pancreas, liver and the gut. CF is caused by cystic fibrosis transmembrane conductance regulator (CFTR) dysfunction, leading to impaired chloride ion transport across membranes [1, 2.

Fields of Study & Subjects

Cystic Fibrosis Research Advances Endoplasmic Reticulum Stress and Disease Occupational and environmental lung diseases

Publication details

Journal / source
European Respiratory Journal
Publisher
European Respiratory Society (ERS)
Volume
67
Issue
6
Pages
2600247–2600247
Publication date
1 June 2026
Language
EN